Levine Media Group’s Daniel Levine will moderate a series of master classes on therapeutic modalities during the Global Genes’ 2023 RARE Advocacy Summit at the Sheraton San Deigo Hoel & Marina. The master class will cover small molecules and biologics, RNA therapies, gene therapy and gene editing, and a case study of therapies for spinal muscular atrophy.
You can view a replay of the sessions here:
Rare Disease Master Class-Tech Innvation: Small Molecule Drugs and Repurposing with Alex Burgin, direction of the Center for the Development of Therapeutics at the Broad Institute
Rare Disease Master Class-Tech Innvation: RNA Therapies: ASOs, mRNAs, and siRNAs with Chris Hart, CEO and president of Creyon Bio; and Rachel Groppo, replicon team lead for Janssen
Rare Disease Master Class-Tech Innvation: Gene Replacement and Gene Editing Therapies with Matthew Fuller, executive director of gene therapy research for Ultragenyx; and Amy Raymond, therapeutic strategy Lead in rare diseases and cellular and genetic medicines for Worldwide Clinical Trials